Key Points New target genes for γ-globin induction identified among all current potential therapeutic agents in an erythroid-biased CRISPR screen. Top novel drug candidates and pathways for fetal hemoglobin induction… Click to show full abstract
Key Points New target genes for γ-globin induction identified among all current potential therapeutic agents in an erythroid-biased CRISPR screen. Top novel drug candidates and pathways for fetal hemoglobin induction examined and validated.
               
Click one of the above tabs to view related content.