This issue of the Croatian Medical Journal (CMJ) features two articles on rare diseases: one dealing with primary biliary cholangitis (1) and the other with muscular dystrophy and spinal muscular… Click to show full abstract
This issue of the Croatian Medical Journal (CMJ) features two articles on rare diseases: one dealing with primary biliary cholangitis (1) and the other with muscular dystrophy and spinal muscular atrophy (SMA) (2). At the CMJ editorial board meeting, these articles have generated considerable discussions about problems regarding research and health policies on rare diseases, particularly in a relatively small country such as Croatia.
               
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