Prevalence of Anti-AAV9 Antibodies in Adult Patients with Spinal Muscular Atrophy.
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DOI: 10.1089/hum.2022.054
Abstract: 5q-associated spinal muscular atrophy (SMA) is an autosomal recessive neuromuscular disorder that leads to progressive muscle atrophy and weakness. The disease is caused by a homozygous deletion or mutation in the survival of motor neuron… read more here.
Keywords: anti aav9; aav9 antibodies; adult patients; aav9 ... See more keywords