Biochemical and clinical biomarkers in adult SMA 3–4 patients treated with nusinersen for 22 months
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DOI: 10.1002/acn3.51625
Abstract: To investigate biomarkers of disease progression in cerebrospinal fluid (CSF) and serum in adult patients with spinal muscular atrophy (SMA). Furthermore, we assess the clinical response to nusinersen treatment in adults with SMA over a… read more here.
Keywords: adult sma; biochemical clinical; clinical biomarkers; patients treated ... See more keywords