Recent Advances in Gene Therapy for Cancer Theranostics.
Sign Up to like & getrecommendations! Published in 2021 at "Current opinion in biomedical engineering"
DOI: 10.1016/j.cobme.2021.100300
Abstract: There is great interest in developing gene therapies for many disease indications, including cancer. However, successful delivery of nucleic acids to tumor cells is a major challenge, and in vivo efficacy is difficult to predict.… read more here.
Keywords: therapy; cancer theranostics; advances gene; cancer ... See more keywords
Advances in gene therapy for Wolfram syndrome
Sign Up to like & getrecommendations! Published in 2017 at "Acta Ophthalmologica"
DOI: 10.1111/j.1755-3768.2017.03174
Abstract: Summary The Wolfram Syndrome (WS) is an early onset genetic disease (1/200 000) featuring diabetes mellitus and progressive optic neuropathy ensuing mutations in the WFS1 gene. To date, there is no treatment to stop the… read more here.
Keywords: therapy wolfram; gene therapy; wolfram syndrome; gene ... See more keywords
Challenges and Advances in Gene Therapy Approaches for Neurodegenerative Disorders.
Sign Up to like & getrecommendations! Published in 2017 at "Current gene therapy"
DOI: 10.2174/1566523217666171013124150
Abstract: INTRODUCTION The recent approval of Spinraza (nusinersen), an antisense oligonucleotide, by U.S. Food and Drug Administration to treat patients with spinal muscular atrophy, has reignited interests of researchers in designing and testing new gene therapy… read more here.
Keywords: gene therapy; therapy approaches; therapy; challenges advances ... See more keywords