Advances in therapies for neurological Lysosomal Storage Disorders.
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DOI: 10.1002/jimd.12615
Abstract: Lysosomal Storage Disorders (LSDs) are a diverse group of inherited, monogenic diseases caused by functional defects in specific lysosomal proteins. The lysosome is a cellular organelle that plays a critical role in catabolism of waste… read more here.
Keywords: therapies neurological; storage disorders; neurological lysosomal; lysosomal storage ... See more keywords