Articles with "ataluren eye" as a keyword



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Formulation and Stability of Ataluren Eye Drop Oily Solution for Aniridia

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Published in 2020 at "Pharmaceutics"

DOI: 10.3390/pharmaceutics13010007

Abstract: Congenital aniridia is a rare and severe panocular disease characterized by a complete or partial iris defect clinically detectable at birth. The most common form of aniridia occurring in around 90% of cases is caused… read more here.

Keywords: stability ataluren; formulation; eye drop; ataluren eye ... See more keywords