Antisense oligonucleotides as a potential treatment for brain deficits observed in myotonic dystrophy type 1.
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DOI: 10.1038/s41434-022-00316-7
Abstract: Myotonic dystrophy, or dystrophia myotonica type 1 (DM1), is a multi-systemic disorder and is the most common adult form of muscular dystrophy. It affects not only muscles but also many organs, including the brain. Cerebral… read more here.
Keywords: antisense; brain; myotonic dystrophy; brain deficits ... See more keywords