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Published in 2019 at "Orphanet Journal of Rare Diseases"
DOI: 10.1186/s13023-019-1149-7
Abstract: BackgroundWolfram syndrome is a rare genetic, progressive, neurodegenerative disorder characterised by childhood-onset diabetes mellitus, diabetes insipidus, optic atrophy and deafness. To date, the economic burden of Wolfram syndrome has not been well-studied or reported. The…
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Keywords:
burden wolfram;
wolfram syndrome;
diabetes mellitus;
cost ... See more keywords