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Published in 2020 at "ESC Heart Failure"
DOI: 10.1002/ehf2.12647
Abstract: Long‐term treatment effect studies in large female Fabry patient groups are challenging to design because of phenotype heterogeneity and lack of appropriate comparison groups, and have not been reported. We compared long‐term cardiomyopathy and kidney…
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Keywords:
cardiomyopathy kidney;
treatment;
agalsidase beta;
female fabry ... See more keywords