Presymptomatic Lesion in Childhood Cerebral Adrenoleukodystrophy
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DOI: 10.1212/wnl.0000000000200571
Abstract: Background and Objectives We sought to characterize the natural history and standard-of-care practices between the radiologic appearance of brain lesions, the appearance of lesional enhancement, and treatment with hematopoietic stem-cell transplant or gene therapy among… read more here.
Keywords: enhancement treatment; time; lesional enhancement; ccald ... See more keywords
Presymptomatic Lesion in Childhood Cerebral Adrenoleukodystrophy: Timing and Treatment.
Sign Up to like & getrecommendations! Published in 2022 at "Neurology"
DOI: 10.1212/wnl.0000000000201440
Abstract: Background and Objectives We sought to characterize the natural history and standard-of-care practices between the radiologic appearance of brain lesions, the appearance of lesional enhancement, and treatment with hematopoietic stem-cell transplant or gene therapy among… read more here.
Keywords: ccald; childhood; cerebral adrenoleukodystrophy; lesion ... See more keywords