Long term survival and cardiopulmonary outcome in children with Hurler syndrome after haematopoietic stem cell transplantation
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DOI: 10.1007/s10545-017-0034-6
Abstract: Premature death in untreated children with Hurler syndrome (HS) in the first decade of life is largely due to life-threatening cardiopulmonary complications. We examined the long-term survival and cardiopulmonary outcome in 54 children undergoing haematopoietic… read more here.
Keywords: outcome; term; hurler syndrome; children hurler ... See more keywords