Mutation-Independent Gene Therapies for Rod-Cone Dystrophies.
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DOI: 10.1007/978-3-319-75402-4_10
Abstract: The clinical success of gene replacement therapies in recent years has served as a proof of concept for the treatment of inherited retinal degenerations using adeno-associated virus (AAV) as viral vector. However, inherited retinal degenerative… read more here.
Keywords: mutation independent; cone dystrophies; rod cone; gene ... See more keywords