Delivery is key: lessons learnt from developing splice‐switching antisense therapies
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DOI: 10.15252/emmm.201607199
Abstract: The use of splice‐switching antisense therapy is highly promising, with a wealth of pre‐clinical data and numerous clinical trials ongoing. Nevertheless, its potential to treat a variety of disorders has yet to be realized. The… read more here.
Keywords: key lessons; delivery; splice switching; delivery key ... See more keywords