Drug Development for Rare Paediatric Epilepsies: Current State and Future Directions
Sign Up to like & getrecommendations! Published in 2019 at "Drugs"
DOI: 10.1007/s40265-019-01223-9
Abstract: Rare diseases provide a challenge in the evaluation of new therapies. However, orphan drug development is of increasing interest because of the legislation enabling facilitated support by regulatory agencies through scientific advice, and the protection… read more here.
Keywords: drug development; development rare; drug; orphan drug ... See more keywords
Research advances in treatment methods and drug development for rare diseases
Sign Up to like & getrecommendations! Published in 2022 at "Frontiers in Pharmacology"
DOI: 10.3389/fphar.2022.971541
Abstract: As the incidence of rare diseases increases each year, the total number of rare disease patients worldwide is nearly 400 million. Orphan medications are drugs used to treat rare diseases. Orphan drugs, however, are rare… read more here.
Keywords: rare diseases; development rare; treatment; drug ... See more keywords