Gene therapy for neurological disorders: progress and prospects
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DOI: 10.1038/nrd.2018.110
Abstract: Adeno-associated viral (AAV) vectors are a rapidly emerging gene therapy platform for the treatment of neurological diseases. In preclinical studies, transgenes encoding therapeutic proteins, microRNAs, antibodies or gene-editing machinery have been successfully delivered to the… read more here.
Keywords: disorders progress; progress prospects; neurological disorders; therapy neurological ... See more keywords