Double dose alglucosidase-alpha doubles benefit?
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DOI: 10.1016/j.ymgmr.2018.07.004
Abstract: We read with interst the article by Landis et al. about a 3 monthsold male with dilated cardiomyopathy due to infantile onset Pompe disease (IOPD) who profited from increased dosage of algucosidase-alpha (40mg/kg/d twice a… read more here.
Keywords: index; dose alglucosidase; case; double dose ... See more keywords