ELX-02: an investigational read-through agent for the treatment of nonsense mutation-related genetic disease
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DOI: 10.1080/13543784.2020.1828862
Abstract: ABSTRACT Introduction ELX-02, an investigational compound that is structurally an aminoglycoside analog, induces read-through of nonsense mutations through interaction with the ribosome, through which full-length functional proteins can be produced. It is being developed as… read more here.
Keywords: treatment; elx investigational; disease; read agent ... See more keywords