Articles with "engage trial" as a keyword



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Clinical outcomes after 4.5 years of eliglustat therapy for Gaucher disease type 1: Phase 3 ENGAGE trial final results

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Published in 2021 at "American Journal of Hematology"

DOI: 10.1002/ajh.26276

Abstract: Eliglustat, an oral substrate reduction therapy, is approved for eligible adults with Gaucher disease type 1. In the Phase 3 ENGAGE trial of previously untreated adults with Gaucher disease type 1, eliglustat‐treated patients had statistically… read more here.

Keywords: disease type; engage trial; gaucher disease; disease ... See more keywords