Evolution of bulbar function in spinal muscular atrophy type 1 treated with nusinersen.
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DOI: 10.1111/dmcn.15171
Abstract: AIM To assess the evolution of bulbar function in nusinersen-treated spinal muscular atrophy type 1 (SMA1). METHOD This single-centre retrospective study identified 24 patients (14 females and 10 males) with SMA1, treated with nusinersen between… read more here.
Keywords: muscular atrophy; bulbar function; bulbar; evolution bulbar ... See more keywords