Expansion of Splice-Switching Therapy with Antisense Oligonucleotides
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DOI: 10.3390/ijms26052270
Abstract: Since 2016, splice-switching therapy, in which splicing is controlled by antisense oligonucleotides, has been applied in clinical practice for spinal muscular atrophy and Duchenne muscular dystrophy. In the former disease, this therapy induces exon inclusion,… read more here.
Keywords: therapy; splice switching; switching therapy; antisense oligonucleotides ... See more keywords