Gene therapeutics for surfactant dysfunction disorders: Targeting the alveolar type 2 epithelial cell.
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DOI: 10.1089/hum.2022.130
Abstract: Genetic disorders of surfactant dysfunction result in significant morbidity and mortality, among infants, children, and adults. Available medical interventions are limited, non-specific and generally ineffective. As such, the need for effective therapies remains. Pathogenic variants… read more here.
Keywords: alveolar type; gene; surfactant dysfunction; gene therapeutics ... See more keywords