Generalizable features of pegRNA design for prime editing of inherited retinal diseases.
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DOI: 10.1080/13816810.2025.2576786
Abstract: BACKGROUND AND OBJECTIVES The variety of ocular cell types involved in inherited retinal disease (IRD) necessitates the use of gene editing therapeutics which have generalizable components. In our study, we investigate the generalizable characteristics of… read more here.
Keywords: non engineered; pegrna design; engineered pegrna; generalizable features ... See more keywords