Gene therapy for hemophilia: what does the future hold?
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DOI: 10.1177/2040620718791933
Abstract: Recent phase I/II adeno-associated viral vector-mediated gene therapy clinical trials have reported remarkable success in ameliorating disease phenotype in hemophilia A and B. These trials, which highlight the challenges overcome through decades of preclinical and… read more here.
Keywords: therapy hemophilia; future hold; gene therapy; hemophilia future ... See more keywords