Natural history and survival rate of familial amyloidosis with polyneuropathy: A nationwide databank
Sign Up to like & getrecommendations! Published in 2023 at "Annals of Clinical and Translational Neurology"
DOI: 10.1002/acn3.51765
Abstract: Hereditary amyloid transthyretin (ATTRv) amyloidosis with polyneuropathy, a rare autosomal‐dominant disease, has gained attention in recent years owing to treatment improvements. However, epidemiological real‐world mega database of nationwide natural history and survival rates, especially with… read more here.
Keywords: natural history; amyloidosis polyneuropathy; history survival;
Reader response: Natural history and survival in stage 1 Val30Met transthyretin familial amyloid polyneuropathy
Sign Up to like & getrecommendations! Published in 2019 at "Neurology"
DOI: 10.1212/wnl.0000000000007870
Abstract: In an observational study conducted in a single country, Coelho et al.1 reported favorable survival of patients with transthyretin familial amyloidosis polyneuropathy (TTR-FAP) who underwent liver transplantation (LTx) or received tafamidis. This report is important… read more here.
Keywords: natural history; response natural; history survival; reader response ... See more keywords