A voice for orphans
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DOI: 10.1038/laban.1335
Abstract: of Sanfilippo, are candidates for enzyme replacement therapy and are currently in clinical trials. But for Jonah’s Type C version, Wood recalls having to start from scratch. “When Jonah was diagnosed, there was nothing happening… read more here.
Keywords: jonah; disease; voice orphans; sanfilippo ... See more keywords