The changing therapeutic landscape of spinal muscular atrophy.
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DOI: 10.31128/ajgp-03-21-5924
Abstract: BACKGROUND The clinical approach to spinal muscular atrophy (SMA) has changed, and the condition is now a treatable neurodegenerative disease, with treated infants and children experiencing gains in motor function and significant increases in survival.… read more here.
Keywords: spinal muscular; landscape spinal; therapeutic landscape; muscular atrophy ... See more keywords