Preliminary development of proxy-rated quality-of-life scales for children and adults with Niemann-Pick type C
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DOI: 10.1007/s11136-019-02234-5
Abstract: Niemann-Pick disease type C (NPC) is a rare life-limiting disease for which there is no cure. No scales currently exist to measure the impact of medication, physical therapy or clinical trials. The aim of this… read more here.
Keywords: children adults; quality life; life; living npc ... See more keywords