Crigler-Najjar syndrome: looking to the future does not make us forget the present
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DOI: 10.1186/s13023-024-03108-x
Abstract: Recently, the safety and efficacy of gene therapy were evaluated in patients with Crigler-Najjar syndrome (CNS). Although it is a promising curative option for CNS, many doubts still persist about its long-term efficacy and safety.… read more here.
Keywords: crigler najjar; najjar syndrome; future make; looking future ... See more keywords