Pathways to establishing managed access and networks of reserves
Sign Up to like & getrecommendations! Published in 2021 at "Marine Policy"
DOI: 10.1016/j.marpol.2021.104580
Abstract: Abstract The specification of user rights and the devolution of fisheries management and allocation decisions to the local fisher and community level has been found to be an effective approach to improved fisheries management. Rare’s… read more here.
Keywords: access networks; networks reserves; access; establishing managed ... See more keywords
Impact of long-term elosulfase alfa treatment on clinical and patient-reported outcomes in patients with mucopolysaccharidosis type IVA: results from a Managed Access Agreement in England
Sign Up to like & getrecommendations! Published in 2021 at "Orphanet Journal of Rare Diseases"
DOI: 10.1186/s13023-021-01675-x
Abstract: Background We present baseline characteristics and follow-up data of a Managed Access Agreement (MAA), including patients with mucopolysaccharidosis IVA (MPS IVA) receiving elosulfase alfa enzyme replacement therapy (ERT) in England on a conditional basis. Patients… read more here.
Keywords: access agreement; patients mucopolysaccharidosis; treatment; clinical patient ... See more keywords
An approach to data collection in compassionate use/managed access
Sign Up to like & getrecommendations! Published in 2022 at "Frontiers in Pharmacology"
DOI: 10.3389/fphar.2022.1095860
Abstract: Compassionate Use (CU)/Managed Access programs provide access to locally unapproved medicines. As these programs become more global and involve a broader range of products, determining whether patients derive benefit from treatment could provide insights into… read more here.
Keywords: managed access; use managed; compassionate use; access ... See more keywords