Migalastat pharmacokinetic (PK) exposure comparisons between race/ethnic groups and between males and females are similar
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DOI: 10.1016/j.ymgme.2018.12.197
Abstract: Fabry disease is an X-linked lysosomal storage disorder caused by a mutation in the GLA gene, resulting in the functional deficiency of α-galactosidase A (α-Gal A). Migalastat is a pharmacological chaperone that binds to and stabilizes amenable forms of… read more here.
Keywords: race; males females; migalastat pharmacokinetic; test ... See more keywords