Minimal clinically important difference for the 6-min walk test: literature review and application to Morquio A syndrome
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DOI: 10.1186/s13023-017-0633-1
Abstract: Morquio A syndrome is an ultra-rare, inherited lysosomal storage disorder associated with progressive, multi-systemic clinical impairments, causing gradual loss of functional capacity and endurance, impaired quality of life, and early mortality. Studies in Morquio A… read more here.
Keywords: min walk; morquio syndrome; morquio patients; review ... See more keywords