Never‐Treated, Non Splenectomised Patients With Gaucher Disease (The French GANT Study): The Prospective Follow‐Up
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DOI: 10.1002/jimd.70026
Abstract: Treatment options for Type 1 Gaucher Disease (GD1) include enzyme replacement therapy and oral substrate reduction therapy. The criteria for treatment initiation vary across regions. Recent retrospective studies have highlighted the natural progression of never‐treated… read more here.
Keywords: never treated; non splenectomised; prospective follow; gaucher disease ... See more keywords