The Onpattro story and the clinical translation of nanomedicines containing nucleic acid-based drugs
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DOI: 10.1038/s41565-019-0591-y
Abstract: The regulatory approval of Onpattro, a lipid nanoparticle-based short interfering RNA drug for the treatment of polyneuropathies induced by hereditary transthyretin amyloidosis, paves the way for clinical development of many nucleic acid-based therapies enabled by… read more here.
Keywords: acid based; onpattro story; clinical translation; story clinical ... See more keywords