Pegvaliase: a novel treatment option for adults with phenylketonuria
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DOI: 10.1080/03007995.2018.1528215
Abstract: Abstract Objective: In May 2018, the US Food and Drug Administration approved pegvaliase-pqpz (Palynziq*), the first enzyme substitution therapy for the treatment of phenylketonuria (PKU). This article provides an overview of the mechanism of action,… read more here.
Keywords: treatment option; pegvaliase; treatment; pegvaliase novel ... See more keywords