Orphan Medicines for Pediatric Use: A Focus on the European Union.
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DOI: 10.1016/j.clinthera.2019.10.006
Abstract: PURPOSE European policy makers have provided a number of incentives for the development of medicines for orphan diseases as early as 1999 through the Orphan Regulation and created obligations for medicines developers to investigate their… read more here.
Keywords: medicines pediatric; european union; orphan medicines; development ... See more keywords
Public spending on orphan medicines: a review of the literature
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DOI: 10.1186/s40545-020-00260-0
Abstract: Background and objective Little is known about how much public payers spend on orphan medicines. This study aimed at identifying information on orphan medicine expenditure incurred by public payers that was published in literature globally… read more here.
Keywords: spending orphan; public spending; orphan medicines; spending ... See more keywords