Overview of Retinal Gene Therapy: Current Status and Future Challenges.
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DOI: 10.1101/cshperspect.a041278
Abstract: The success of the first Food and Drug Administration (FDA)- and European Medicines Agency (EMA)-approved gene therapy for genetic disease, voretigene neparovovec-rzyl, (Luxturna) has helped pave the way for development of retinal gene therapies to… read more here.
Keywords: therapy current; overview retinal; gene therapy; gene ... See more keywords