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Published in 2023 at "Journal of neuromuscular diseases"
DOI: 10.3233/jnd-230019
Abstract: BACKGROUND Duchenne muscular dystrophy (DMD) is a neuromuscular disease stemming from dystrophin gene mutations. Lack of dystrophin leads to progressive muscle damage and replacement of muscle with fibrotic and adipose tissue. Pamrevlumab (FG-3019), a fully…
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Keywords:
duchenne muscular;
ambulatory patients;
pamrevlumab;
non ambulatory ... See more keywords