Pharmaceutical Chaperones and Proteostasis Regulators in the Therapy of Lysosomal Storage Disorders: Current Perspective and Future Promises
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DOI: 10.3389/fphar.2017.00448
Abstract: Different approaches have been utilized or proposed for the treatment of lysosomal storage disorders (LSDs) including enzyme replacement and hematopoietic stem cell transplant therapies, both aiming to compensate for the enzymatic loss of the underlying… read more here.
Keywords: proteostasis regulators; lysosomal storage; proteostasis; pharmaceutical chaperones ... See more keywords