Postnatal gene therapy for neuromuscular diseases – opportunities and limitations
Sign Up to like & getrecommendations! Published in 2021 at "Journal of Perinatal Medicine"
DOI: 10.1515/jpm-2021-0435
Abstract: Abstract During the last decade a number of innovative treatments including gene therapies have been approved for the treatment of monogenic inherited diseases. For some neuromuscular diseases these approaches have dramatically changed the course of… read more here.
Keywords: neuromuscular diseases; postnatal gene; diseases opportunities; therapy neuromuscular ... See more keywords