Therapeutic Prospects for Friedreich's Ataxia.
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DOI: 10.1016/j.tips.2019.02.001
Abstract: Friedreich's ataxia (FRDA) is a progressive disease affecting multiple organs that is caused by systemic insufficiency of the mitochondrial protein frataxin. Current therapeutic strategies aim to elevate frataxin levels and/or alleviate the consequences of frataxin… read more here.
Keywords: friedreich ataxia; therapeutic prospects; prospects friedreich;