Combination of a TGF‐β ligand trap (RAP‐GRL) and TMPRSS6‐ASO is superior for correcting β‐thalassemia
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DOI: 10.1002/ajh.27332
Abstract: A recently approved drug that induces erythroid cell maturation (luspatercept) has been shown to improve anemia and reduce the need for blood transfusion in non‐transfusion‐dependent as well as transfusion‐dependent β‐thalassemia (BT) patients. Although these results… read more here.
Keywords: iron; rap grl; tmprss6 aso; transfusion ... See more keywords