Responsiveness of the SARA and natural history in 884 recessive and early onset ataxia patients.
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DOI: 10.1002/ana.26712
Abstract: OBJECTIVE The Scale for the Assessment and Rating of Ataxia (SARA) is the most widely applied clinical outcome assessment (COA) for genetic ataxias, but presents metrological and regulatory challenges. To facilitate trial planning, we characterize… read more here.
Keywords: natural history; sara; early onset; recessive early ... See more keywords