Articles with "repositioning thalassemia" as a keyword



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A Rational Approach to Drug Repositioning in β-thalassemia: Induction of Fetal Hemoglobin by Established Drugs

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Published in 2022 at "Wellcome Open Research"

DOI: 10.12688/wellcomeopenres.17845.3

Abstract: Drug repositioning and the relevance of orphan drug designation for β-thalassemia is reviewed. Drug repositioning and similar terms ('drug repurposing', 'drug reprofiling', 'drug redirecting', ‘drug rescue’, ‘drug re-tasking’ and/or 'drug rediscovery') have gained great attention,… read more here.

Keywords: rational approach; approach drug; drug repositioning; repositioning thalassemia ... See more keywords