Fusion of RVG or gh625 to Iduronate-2-Sulfatase for the Treatment of Mucopolysaccharidosis Type II.
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DOI: 10.1089/hum.2023.025
Abstract: Mucopolysaccharidosis type II (MPSII) is a lysosomal storage disease caused by a mutation in the IDS gene, resulting in deficiency of the enzyme iduronate-2-sulfatase (IDS) causing heparan sulfate (HS) and dermatan sulfate (DS) accumulation in… read more here.
Keywords: iduronate sulfatase; rvg gh625; mucopolysaccharidosis type; type ... See more keywords