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Published in 2023 at "Science"
DOI: 10.1126/science.adi8792
Abstract: Description FDA is expected to endorse Duchenne muscular dystrophy treatment, as safety concerns linger over uses of viruses FDA is expected to endorse Duchenne muscular dystrophy treatment, as safety concerns linger over uses of viruses
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Keywords:
milestone looms;
gene therapy;
field seeks;
seeks better ... See more keywords