An evaluation of the combination of sodium phenylbutyrate and taurursodiol for the treatment of amyotrophic lateral sclerosis
Sign Up to like & getrecommendations! Published in 2023 at "Expert Review of Neurotherapeutics"
DOI: 10.1080/14737175.2023.2174018
Abstract: ABSTRACT Introduction Amyotrophic lateral sclerosis (ALS) is a rapidly progressive, fatal neurodegenerative motor neuron disease. Despite the overwhelming need for effective therapeutics for ALS, riluzole and edaravone were the only two FDA-approved disease-modifying therapies prior… read more here.
Keywords: phenylbutyrate taurursodiol; sodium phenylbutyrate; amyotrophic lateral;
Profile of sodium phenylbutyrate granules for the treatment of urea-cycle disorders: patient perspectives
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DOI: 10.2147/ppa.s136754
Abstract: Urea-cycle disorders are a group of rare hereditary metabolic diseases characterized by deficiencies of one of the enzymes and transporters involved in the urea cycle, which is necessary for the removal of nitrogen produced from… read more here.
Keywords: cycle disorders; sodium phenylbutyrate; urea cycle; sodium ... See more keywords