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Published in 2024 at "Advances in Therapy"
DOI: 10.1007/s12325-024-02782-4
Abstract: Rett syndrome (RTT) is a rare genetic neurodevelopmental disorder mainly affecting female individuals. Trofinetide was recently approved as the first treatment for RTT, largely on the basis of results from the phase 3 LAVENDER trial,…
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Keywords:
treatment;
trofinetide;
symptoms resulting;
rett syndrome ... See more keywords