Targeted enzyme delivery systems in lysosomal disorders: an innovative form of therapy for mucopolysaccharidosis
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DOI: 10.1007/s00018-019-03135-z
Abstract: Mucopolysaccharidoses (MPSs), which are inherited lysosomal storage disorders caused by the accumulation of undegraded glycosaminoglycans, can affect the central nervous system (CNS) and elicit cognitive and behavioral issues. Currently used enzyme replacement therapy methodologies often… read more here.
Keywords: targeted enzyme; systems lysosomal; delivery systems; enzyme delivery ... See more keywords