Advancements in therapeutics for inborn errors of metabolism
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DOI: 10.1097/mop.0000000000001168
Abstract: Purpose of review To present new therapeutic modalities for inborn errors of metabolism that are in clinical trials or recently approved by the US Food and Drug Administration (FDA) and to improve pediatricians’ understanding of… read more here.
Keywords: advancements therapeutics; errors metabolism; inborn errors; new therapies ... See more keywords